https://www.selleckchem.com/pr....oducts/sodium-l-asco
Treatment was deemed effective in 79 of 85 patients (92.9%, 95% CI 85.3-97.4). One (1.2%) patient experienced an adverse drug reaction (alanine aminotransferase increased) 50 days after the start of administration, which resolved without complications with continued treatment. Sapropterin appears well tolerated and highly effective in Japanese patients treated in a real-world setting, including those who start treatment at age 4 years and pregnant women. Sapropterin appears well tolerated and highly effective i